ACD hosted an Externally-Led Patient Focused Drug Development (EL-PFDD) meeting on Cerebral Creatine Deficiency Syndromes (CCDS) on January 24, 2023. This meeting provided an important opportunity for patients and caregivers to inform FDA representatives, academic and scientific researchers, medical professionals, and pharmaceutical companies about personal experiences regarding the symptoms and daily impact of CCDS, as well as thoughts on current and future approaches to therapies.
The transcript of the meeting is available below. The CCDS Voice of the Patient Report will be completed and posted here in spring of 2023.